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Publication
PropertyValue
Working Groups RG Cyganek, RG Hasenfuß, RG Wollnik, RG Zelarayán-Behrend, RG Zimmermann
SubprojectNone
Open AccessOpen Access Yes
Publication TypeJournal Article
Peer ReviewedYes
PMIDPubMed ID 38333672
DOIDOI 10.1016/j.omtn.2024.102123
Publication Year2024
TitlePreclinical evaluation of CRISPR-based therapies for Noonan syndrome caused by deep-intronic LZTR1 variants
JournalMolecular Therapy-Nucleic Acids
ISSN2162-2531
eISSN2162-2531
URL http://dx.doi.org/10.1016/j.omtn.2024.102123
Pages102123
Issue1
Volume35
Journal AbbreviationMol Ther-Nucl Acids
AuthorsKnauer C, Haltern H, Schoger E, Kügler S, Roos L, Zelarayán LC, Hasenfuss G, Zimmermann W, Wollnik B, Cyganek L
First AuthorKnauer C
Last AuthorCyganek L

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 scienced...in.pdf  Article fulltext

 gro-2/141877  GRO.publications identifier

 0000-0002-5485-9828  ORCID identifier (Eric Schoger)

 0000-0002-5130-2012  ORCID identifier (Sebastian Kügler)

 0000-0002-9001-0346  ORCID identifier (Laura Cecilia Zelarayán-Behrend)

 0000-0002-5942-361X  ORCID identifier (Gerd Hasenfuß)

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 0000-0003-2589-0364  ORCID identifier (Bernd Wollnik)

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 ars.els-...c1.pdf  Supplemental material

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