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Publication
Property Value
Working Groups RG Fischer, RG Gärtner
Subproject None
Open Access Open Access  Yes
Publication Type Congresses
Peer Reviewed Unknown
DOI DOI  10.1055/s-0043-1777171
Publication Year 2023
Title Tazarotene and Bexarotene Show Efficacy as In Vitro Therapeutic Agents in Multiple Sulfatase Deficiency
Journal Neuropediatrics
ISSN 0174-304X
eISSN 1439-1899
URL  https://www.thieme-connect.com/products/ejournals/html/10.1055/s-0043-1777171#info
Pages S1-S32
Issue S 01
Volume 54
Journal Abbreviation Neuropediatrics
Authors Schlotawa L, Matysiak K, Kettwig M, Ahrens-Nicklas RC, Baud M, Berulava T, Brunetti-Pierri N, Gagne A, Herbst ZM, Maguire JA, Monfregola J, Pena T, Radhakrishnan K, Schröder S, Waxman EA, Ballabio A, Dierks T, Fischer A, French DL, Gelb MH, Gärtner J
First Author Schlotawa L
Last Author Gärtner J

 External Resources

 272200 OMIM identifier (272200, Multiple Sulfatase Deficiency; MSD)

 0000-0002-7415-4905 ORCID identifier (Lars Schlotawa)

 0000-0003-4804-7716 ORCID identifier (Matthias Kettwig)

 0000-0002-9329-8912 ORCID identifier (Tonatiuh Peña-Centeno)

 0000-0003-4562-7969 ORCID identifier (Elisa A. Waxman)

 0000-0001-8546-1161 ORCID identifier (André Fischer)

 0000-0003-4108-7109 ORCID identifier (Jutta Gärtner)

 02pttbw34 ROR identifier (02pttbw34, Baylor College of Medicine)

 02hpadn98 ROR identifier (02hpadn98, Bielefeld University)

 01z7r7q48 ROR identifier (01z7r7q48, Children's Hospital of Philadelphia)

 043j0f473 ROR identifier (043j0f473, German Center for Neurodegenerative Diseases)

 05xy1nn52 ROR identifier (05xy1nn52, Multiscale Bioimaging)

 04xfdsg27 ROR identifier (04xfdsg27, Telethon Institute Of Genetics And Medicine)

 021ft0n22 ROR identifier (021ft0n22, University Medical Center Göttingen)

 05290cv24 ROR identifier (05290cv24, University of Naples Federico II)

 01ryk1543 ROR identifier (01ryk1543, University of Southampton)

 00cvxb145 ROR identifier (00cvxb145, University of Washington)

 mbexc.de...iency/ Website entry (mbexc.de)

 mbexc.de...iency/ Website entry (mbexc.de)